Review
Open access
Jul 2026
Duchenne muscular dystrophy: from gene to gene-ius therapies
Recent advances in DMD management represent a paradigm shift in DMD management and offer renewed hope for improving survival and quality of life for affected individuals, and future directions in therapeutic development are considered.
Antoine Muchir, A. Musarò, Jeffrey S. Chamberlain
· Skeletal Muscle · 0 citations