Future-proofing thalassaemia care: harnessing scalable therapies, artificial intelligence, and global collaboration.
Advances in the treatment of thalassaemia have led to major improvements in survival and quality of life over the past 30 years. In addition to developments in stem-cell transplantation, transfusion safety, iron overload monitoring, and iron-chelation therapy, novel disease-modifying and gene therapies are also emergin...