Jul 2026
Huntingtin is a cell-autonomous regulator of neuropeptide trafficking and clock output
Through targeted genetic knock-down, huntingtin is identified as a cell-autonomous regulator of neuropeptide trafficking, neuronal excitability and circadian output and carries direct relevance for HD therapeutic strategies, particularly those involving huntingtin-lowering approaches.
Agustina Bruno-Vignolo, Cayetana Arnaiz, Florencia Fernández-Chiappe et al.
· bioRxiv · 0 citations