Sep 2026
Revisiting Enzyme Replacement Therapy for Aspartylglucosaminuria: Truncated Phosphotransferase Enhances Mannose-6-Phosphorylation and Cellular Uptake of Aspartylglucosaminidase.
A. Banning, Lidia Reznikova, Adla Murad et al.
· Journal of Inherited Metabol... · 0 citations