Open access
Sep 2026
Elexacaftor/tezacaftor/ivacaftor improves CFTR function to near-normal levels in children with cystic fibrosis.
Treatment with ETI results in near-normal CFTR function measured in freshly obtained rectal biopsies in children with CF aged 2 to 11 years and at least one F508del allele, and strong correlations of the cAMP response and the total chloride response with age are observed.
Jasmin Berger, Yin Yu, J. Berges et al.
· European Respiratory Journal · 0 citations