Vivek Mundada

Therapeutic Advances in Duchenne Muscular Dystrophy: Regulatory Milestones, Emerging Modalities, and Implications for Clinical Practice

Duchenne muscular dystrophy (DMD) is undergoing rapid therapeutic change, driven by mutation-specific treatments, gene-based interventions, and non-gene disease-modifying approaches. At the same time, regulatory decisions and emerging safety data increasingly determine which therapies can be used, in which patients, an...