#gene editing
Sep 2026
Novel Therapeutic Frontiers in Duchenne Muscular Dystrophy: Gene Therapy, Exon Skipping, and Stem Cell Approaches.
Through multidisciplinary treatment and continuous scientific progress, individualized precision medicine that integrates therapies targeting secondary pathogenic pathways with dystrophin-restoration techniques can finally convert this devastating illness into a tolerable chronic ailment.
Shahjad Ansari, Mohd Amaan Saifi, Sarfaraz Ahmed et al.
· Current pharmaceutical desig... · 0 citations