Open access
A functional comparison of readthrough agent ELX-02 across a wide range of nonsense CFTR variants
M. Destoop
A. Ramalho
Iris AL. Silva
A. Vonk
S. Suen
M. Bierlaagh
Sylvia F Boj
R. Vries
J. Beekman
K. de Boeck
C. K. van der Ent
Margarida D. Amaral
Francois Vermeulen
S. Spelier
Biology